The first gene therapy given to babies for deadly hereditary diseases.

The U.S. researchers gave genetic therapy with the customized CRISPR gene-editing therapy first time to a human baby. That therapy can be the new path for the next-generation medical treatment that replaces vaccines and medicine with new types of genetic editing. Genetic engineering makes it possible to create individuals that have modified immune defenses. 

The modified immune cells can remove dirt from blood vessels. They can remove unwanted chemicals. Those cells can travel into the wanted position. Then the customized DNA turns them into new cells that can fix damages or remove the unwanted cells. The idea is that the hereditary ill cells will turn into wealth cells by changing the DNA in their nucleus. The problem is how the system selects and makes that change in large numbers of cells. 

That modification can boost the immune cell's ability to recognize and destroy things like zombie cells more effectively. In high-accurate genetic engineering and gene therapy. The system uses enzymes or nutrients that the targeted cell type uses. And then that package transports the new DNA into the targeted cells. The molecular machine destroys the old DNA. 

Then it replaces that DNA using the new, artificial DNA. The artificial DNA is manipulated by connecting the other DNA bites to the new entirety. That thing can make it possible to reprogram cells. In those cases, the system can use the modified "B"-cells that normally create antibodies. If researchers want to give gene therapy to adult people they must be sure, that there is enough DNA and nanomachines that can transport enough DNA to large enough cell groups. 

The ability to manipulate DNA is the thing that makes it possible to transform cells into another. This technology allows to creation of synthetic tissues from skin to nerve tissues. Those systems make it possible to make the "spare parts" for people. And the customized DNA can allow to turn bacteria into the receiver's own cells. There are models where the researchers create customized immune cells in the laboratory. Then those cells produce viruses whose mission is to transport DNA into the selected cells. 

https://interestingengineering.com/health/first-personalized-crispr-gene-therapy